About
Sarepta Therapeutics is a biotechnology company focused on developing precision genetic medicines to treat rare diseases, with a particular emphasis on neuromuscular and central nervous system disorders. The company leverages a range of technologies, including gene therapy, gene editing, and RNA-targeted therapeutics, to address diseases with high unmet medical need. Sarepta’s pipeline includes treatments for Duchenne muscular dystrophy and other rare genetic conditions, aiming to transform the lives of patients through innovative science and a commitment to advancing genetic medicine.
